Tyrosinemia type 1

Orpha code: 882OMIM code: 276700

Definition

Tyrosinemia type 1 (HTI) is an inborn error of tyrosine catabolism caused by defective activity of fumarylacetoacetate hydrolase (FAH) and is characterized by progressive liver disease, renal tubular dysfunction, porphyria-like crises and a dramatic improvement in prognosis following treatment with nitisinone.

Disease data
Classification

Disease

Synonyms
FAH deficiency
Niedobór FAH
Niedobór fumaryloacetoacetazy
Niedobór hydrolazy fumaryloacetooctanu
Tyrozynemia typu I
Tyrozynemia wątrobowo-nerkowa
Fumarylacetoacetase deficiency
Fumarylacetoacetate hydrolase deficiency
Hepatorenal tyrosinemia
Tyrosinemia type I
ORPHA code
882
OMIM code
276700
ICD10 code
E70.2
ICD11 code
5C50.11

No additional description.

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