Microcephaly-intellectual disability-sensorineural hearing loss-epilepsy-abnormal muscle tone syndrome

Orpha code: 457351OMIM code: 616577

Definition

A rare genetic disease characterized by microcephaly, global developmental delay, intellectual disability, abnormal muscle tone, and sensorineural hearing impairment. Additional variable manifestations include epilepsy, cortical visual impairment, gastrointestinal disturbances, growth restriction, scoliosis, as well as immunodeficiency and thrombocytopenia. Brain imaging may show cerebral atrophy, thin corpus callosum, and hypomyelination.

Disease data
Classification

Malformation syndrome

Synonyms
Microcephaly-intellectual disability-sensorineural deafness-epilepsy-abnormal muscle tone syndrome
Zespół małogłowia, niepełnosprawności intelektualnej, głuchoty czuciowo-nerwowej, padaczki i nieprawidłowego napięcia mięśniowego
ORPHA code
457351
OMIM code
616577
ICD10 code
-
ICD11 code
-

No additional description.

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