Progressive retinal dystrophy due to retinol transport defect

Orpha code: 352718OMIM code: 615147

Definicja

Progressive retinal dystrophy due to retinol transport defect is a rare, genetic, metabolite absorption and transport disorder characterized by progressive rod-cone dystrophy, usually presenting with impaired night vision in childhood, progressive loss of visual acuity and severe retinol deficiency without keratomalacia. Association with ocular colobomas, severe acne and hypercholesterolemia has been reported.

Disease data
Klasyfikacja

Disease

Synonimy
Retinol dystrophy-iris coloboma-comedogenic acne syndrome
Zespół dystrofia retinolowa-rozszczep tęczówki-trądzik komedogenny
Kod ORPHA
352718
Kod OMIM
615147
Kod ICD10
H35.5
Kod ICD11
-

No additional description.

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