Nathalie syndrome

Orpha code: 2663OMIM code: 255990

Definition

A rare, genetic developmental defect during embryogenesis disorder characterized by sensorineural hearing impairment, childhood-onset cataract, underdeveloped secondary sexual characteristics, spinal muscular atrophy, growth retardation, and cardiac and skeletal anomalies. Sudden death, as well as fatal cardiomyopathy and heart failure, have been described in some cases.

Disease data
Classification

Malformation syndrome

Synonyms
Deafness-cataract-skeletal anomalies syndrome
Głuchota - zaćma - wady szkieletu
Sensorineural hearing loss-cataract-skeletal anomalies-cardiomyopathy syndrome
ORPHA code
2663
OMIM code
255990
ICD10 code
Q87.8
ICD11 code
-

No additional description.

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