Autosomal recessive spastic paraplegia type 39

Orpha code: 139480OMIM code: 612020

Definicja

A rare autosomal recessive complex spastic paraplegia characterized by upper motor neuron involvement and peripheral neuropathy with an onset between childhood and early adulthood. Patients present with progressive spasticity, hyperreflexia, and distal upper and lower muscle wasting. Reduced cognitive functioning and cerebellar ataxia have also been reported. MR imaging may reveal cerebellar and/or spinal cord atrophy.

Disease data
Klasyfikacja

Disease

Synonimy
SPG39
Paraplegia spastyczna z powodu mutacji NTE
Spastyczna paraplegia z powodu mutacji neuropatycznej esterazy
SPG39
Spastic paraplegia due to NTE mutation
Spastic paraplegia due to neuropathy target esterase mutation
Kod ORPHA
139480
Kod OMIM
612020
Kod ICD10
G11.4
Kod ICD11
8B44.01

No additional description.

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