Neurodegeneration due to 3-hydroxyisobutyryl-CoA hydrolase deficiency

Orpha code: 88639OMIM code: 250620

Definicja

Neurodegeneration due to 3-hydroxyisobutyryl-CoA hydrolase deficiency is characterised by delayed motor development, hypotonia and progressive neurodegeneration. To date, it has been described in four boys. The syndrome is caused by mutations affecting the two alleles of the <i> HIBCH</i> gene, encoding 3-hydroxyisobutyryl-CoA hydrolase. The mode of transmission has not yet been established.

Disease data
Klasyfikacja

Disease

Synonimy
HIBCH deficiency
Acyduria metakrylowa
Defekt metabolizmu waliny
Niedobór HIBCH
Methacrylic aciduria
Valine metabolic defect
Kod ORPHA
88639
Kod OMIM
250620
Kod ICD10
E71.1
Kod ICD11
-

No additional description.

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