Neurodegeneration due to 3-hydroxyisobutyryl-CoA hydrolase deficiency

Orpha code: 88639OMIM code: 250620

Definition

Neurodegeneration due to 3-hydroxyisobutyryl-CoA hydrolase deficiency is characterised by delayed motor development, hypotonia and progressive neurodegeneration. To date, it has been described in four boys. The syndrome is caused by mutations affecting the two alleles of the <i> HIBCH</i> gene, encoding 3-hydroxyisobutyryl-CoA hydrolase. The mode of transmission has not yet been established.

Disease data
Classification

Disease

Synonyms
HIBCH deficiency
Acyduria metakrylowa
Defekt metabolizmu waliny
Niedobór HIBCH
Methacrylic aciduria
Valine metabolic defect
ORPHA code
88639
OMIM code
250620
ICD10 code
E71.1
ICD11 code
-

No additional description.

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