Refsum disease

Orpha code: 773OMIM code: 614879

Definition

A metabolic disease characterized by anosmia, cataract, early-onset retinitis pigmentosa and possible neurological manifestations, including peripheral neuropathy and cerebellar ataxia. Other features can be deafness, ichthyosis, skeletal abnormalities, and cardiac arrhythmia. It is characterized biochemically by accumulation of phytanic acid in plasma and tissues.

Disease data
Classification

Disease

Synonyms
Adult Refsum disease
Dziedziczna neuropatia ruchowa i czuciowa typu 4
Heredopathia atactica polyneuritiformis
HMSN 4
Niedobór oksydazy kwasu fitanowego
Classic Refsum disease
HMSN 4
HMSN IV
Hereditary motor and sensory neuropathy type 4
Hereditary motor and sensory neuropathy type IV
Heredopathia atactica polyneuritiformis
Phytanic-CoA hydroxylase deficiency
ORPHA code
773
OMIM code
614879
ICD10 code
G60.1
ICD11 code
5C57.1

No additional description.

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