Mucopolysaccharidosis type 4

Orpha code: 582OMIM code: 253010

Definition

A rare lysosomal storage disease characterized by mild to severe spondylo-epiphyso-metaphyseal dysplasia, manifesting with disproportionate short stature (short neck and trunk), joint laxity, pectus carinatum, genum valgum, abnormal gait, tracheal narrowing, spinal abnormalities (kyphosis and scoliosis), respiratory impairment and valvular heart disease.

Disease data
Classification

Disease

Synonyms
MPS4
Choroba Morquio
MPS4
MPSIV
Mukopolisacharydoza typu IV
MPSIV
Morquio disease
Mucopolysaccharidosis type IV
ORPHA code
582
OMIM code
253010
ICD10 code
E76.2
ICD11 code
5C56.32

No additional description.

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