Megalencephalic leukoencephalopathy with subcortical cysts

Orpha code: 2478OMIM code: 613926

Definition

A form of leukodystrophy that is characterized by infantile-onset macrocephaly, often with mild neurologic signs at presentation (such as mild motor delay), which worsen with time, leading to poor ambulation, falls, ataxia, spasticity, increasing seizures and cognitive decline. Brain magnetic resonance imaging reveals diffusely abnormal and mildly swollen white matter as well as subcortical cysts in the anterior temporal and frontoparietal regions.

Disease data
Classification

Disease

Synonyms
MLC
Leukodystrofia z wielkogłowiem
MLC
Wielkogłowie - leukodystrofia torbielowata
Wielkogłowie z leukodystrofią wakuolizującą i torbielami podkorowymi
Zespół Van der Knaapa
Megalencephalic leukodystrophy
Megalencephaly-cystic leukodystrophy syndrome
Vacuolating megalencephalic leukoencephalopathy with subcortical cysts
Van der Knaap syndrome
ORPHA code
2478
OMIM code
613926
ICD10 code
E75.2
ICD11 code
8A44.3

No additional description.

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