RFT1-CDG

Orpha code: 244310OMIM code: 612015

Definition

RFT1-CDG is a form of congenital disorders of N-linked glycosylation characterized by poorly coordinated suck resulting in difficulty feeding and failure to thrive; myoclonic jerks with hypotonia and brisk reflexes progressing to a seizure disorder; roving eyes; developmental delay; poor to absent visual contact; and sensorineural hearing loss. Additional features that may be observed include coagulation factor abnormalities, inverted nipples and microcephaly. The disease is caused by mutations in the gene <i>RFT1</i> (3p21.1).

Disease data
Classification

Disease

Synonyms
CDG syndrome type In
CDG1N
CDG-In
Niedobór flipazy Man5GlcNAc2-PP-Dol
Wrodzone zaburzenie glikozylacji typu 1n
Wrodzone zaburzenie glikozylacji typu In
Zespół CDG typu In
Zespół obniżonej glikozylacji glikoprotein typu In
CDG-In
CDG1N
Carbohydrate deficient glycoprotein syndrome type In
Congenital disorder of glycosylation type 1n
Congenital disorder of glycosylation type In
Man5GlcNAc2-PP-Dol flippase deficiency
ORPHA code
244310
OMIM code
612015
ICD10 code
E77.8
ICD11 code
5C54.0

No additional description.

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