Cystinosis

Orpha code: 213OMIM code: 219900

Definition

A rare lysosomal disease characterized by an accumulation of cystine inside the lysosomes, causing damage in different organs and tissues, particularly in the kidneys and eyes. Three clinical forms have been described: nephropathic infantile, nephropathic juvenile and ocular.

Disease data
Classification

Disease

Synonyms
Białkowy defekt transportu cystyny
Protein defect of cystin transport
ORPHA code
213
OMIM code
219900
ICD10 code
E72.0
ICD11 code
5C60.1

No additional description.

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