GTP cyclohydrolase I deficiency

Orpha code: 2102OMIM code: 233910

Definition

GTP-cyclohydrolase I deficiency, an autosomal recessive genetic disorder, is one of the causes of malignant hyperphenylalaninemia due to tetrahydrobiopterin deficiency. Not only does tetrahydrobiopterin deficiency cause hyperphenylalaninemia, it is also responsible for defective neurotransmission of monoamines because of malfunctioning tyrosine and tryptophan hydroxylases, both tetrahydrobiopterin-dependent hydroxylases.

Disease data
Classification

Clinical subtype

Synonyms
GTPCH deficiency
Hiperfenylalaninemia spowodowana niedoborem cyklohydrolazy GTP
Niedobór GTPCH
Hyperphenylalaninemia due to GTP cyclohydrolase deficiency
ORPHA code
2102
OMIM code
233910
ICD10 code
E70.1
ICD11 code
5C59.01

No additional description.

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