3-hydroxy-3-methylglutaric aciduria

Orpha code: 20OMIM code: 246450

Definition

A rare organic aciduria, due to deficiency of 3-hydroxy-3-methylglutaryl-CoA lyase characterized by episodes of metabolic decompensation with hypoketotic hypoglycemia triggered by periods of fasting or infections.

Disease data
Classification

Disease

Synonyms
3-hydroxy-3-methylglutaryl-CoA lyase deficiency
Acyduria hydroksymetylglutarowa
Niedobór liazy 3-hydroksy-3-metyloglutaro-CoA
Niedobór liazy HMG-CoA
HMG-CoA lyase deficiency
Hydroxymethylglutaric aciduria
ORPHA code
20
OMIM code
246450
ICD10 code
E71.1
ICD11 code
5C50.E0

No additional description.

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