2-methylbutyryl-CoA dehydrogenase deficiency

Orpha code: 79157OMIM code: 610006

Definition

A rare organic aciduria characterized by impaired isoleucine degradation with increased plasma or whole blood C5 acylcarnitine levels (typically observed in newborn screening) and increased urinary excretion of N-methylbutyrylglycine. The condition is usually clinically asymptomatic, although patients with muscular hypotonia, developmental delay, and seizures (among others) have been reported.

Disease data
Classification

Disease

Synonyms
2-methylbutyric aciduria
Acyduria 2-metylobutyrylowa
Niedobór dehydrogenazy krótkich/rozgałęzionych łańcuchów acylo-CoA
Niedobór SBCAD
Opóźnienie rozwoju z powodu niedoboru dehydrogenazy 2-metylobutyrylo-CoA
Developmental delay due to 2-methylbutyryl-CoA dehydrogenase deficiency
SBCAD deficiency
Short/branched-chain acyl-coA dehydrogenase deficiency
ORPHA code
79157
OMIM code
610006
ICD10 code
E71.1
ICD11 code
-

No additional description.

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