Transketolase deficiency

Orpha code: 488618OMIM code: 617044

Definition

A rare disorder of pentose phosphate metabolism characterized by developmental delay and intellectual disability, delayed or absent speech, short stature, and congenital heart defects (such as ventricular septal defect, atrial septal defect, and patent foramen ovale). Additional reported features include hypotonia, hyperactivity, stereotypic behavior, ophthalmologic abnormalities (bilateral cataract, uveitis, strabismus), hearing impairment, and variable facial dysmorphism, among others. Laboratory analysis shows elevated plasma and urinary polyols (erythritol, arabitol, and ribitol) and urinary sugar-phosphates (ribose-5-phosphate and xylulose/ribulose-5-phosphate).

Disease data
Classification

Malformation syndrome

Synonyms
Short stature-developmental delay-congenital heart defect syndrome
TKT deficiency
Short stature-developmental delay-congenital heart defect syndrome
TKT deficiency
ORPHA code
488618
OMIM code
617044
ICD10 code
E88.8
ICD11 code
-

No additional description.

Orphanet - interntowa baza danych dotyczących rzadkich chorób i sierochych leków. ©INSERM 1999 - Dostępna na stronie www.orphanet.pl