Gamma-sarcoglycan-related limb-girdle muscular dystrophy R5

Orpha code: 353OMIM code: 253700

Definition

A subtype of autosomal recessive limb-girdle muscular dystrophy characterized by a childhood onset of progressive shoulder and pelvic girdle muscle weakness and atrophy frequently associated with calf hypertrophy, diaphragmatic weakness, and/or variable cardiac abnormalities. Mild to moderate elevated serum creatine kinase levels and positive Gowers sign are reported.

Disease data
Classification

Disease

Synonyms
Autosomal recessive limb-girdle muscular dystrophy type 2C
Dystrofia obręczowo-kończynowa z powodu niedoboru gamma-sarkoglikanu
Gamma-sarkoglikanopatia
LGMD2C
Gamma-sarcoglycan-related LGMD R5
Gamma-sarcoglycanopathy
LGMD due to gamma-sarcoglycan deficiency
LGMD type 2C
LGMD2C
Limb-girdle muscular dystrophy due to gamma-sarcoglycan deficiency
Limb-girdle muscular dystrophy type 2C
ORPHA code
353
OMIM code
253700
ICD10 code
-
ICD11 code
8C70.41

No additional description.

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