Dihydropteridine reductase deficiency

Orpha code: 226OMIM code: 261630

Definition

Dihydropteridine reductase (DHPR) deficiency is a severe form of hyperphenylalaninemia (HPA) due to impaired regeneration of tetrahydrobiopterin (BH4) (see this term), leading to decreased levels of neurotransmitters (dopamine, serotonin) and folate in cerebrospinal fluid, and causing neurological symptoms such as psychomotor delay, hypotonia, seizures, abnormal movements, hypersalivation, and swallowing difficulties.

Disease data
Classification

Clinical subtype

Synonyms
Hyperphenylalaninemia due to dihydropteridine reductase deficiency
Fenyloketonuria typu 2
Hiperfenyloalaninemia spowodowana niedoborem reduktazy dihydropterydyny
PKU typu 2
PKU type 2
Phenylketonuria type 2
ORPHA code
226
OMIM code
261630
ICD10 code
E70.1
ICD11 code
5C59.01

No additional description.

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