Beta-ketothiolase deficiency

Orpha code: 134OMIM code: 203750

Definition

A rare, genetic organic aciduria affecting ketone body metabolism and the catabolism of isoleucine and characterized by intermittent ketoacidotic episodes associated with vomiting, dyspnea, tachypnoea, hypotonia, lethargy and coma, with an onset during infancy and usually ceasing by adolescence.

Disease data
Classification

Disease

Synonyms
3-ketothiolase deficiency
Kwasica alfa metyloacetooctowa
Niedobór 3-ketotiolazy
Niedobór 3-oksotiolazy
Niedobór mitochondrialnej tiolazy acetoacetylo-koenzymu A
Niedobór T2
Niedobór tiolazy alfa-metylo-acetoacetylo-CoA
3-oxothiolase deficiency
Alpha methylacetoacetic aciduria
Alpha-methyl-acetoacetyl-CoA thiolase deficiency
Mitochondrial acetoacetyl-coenzyme A thiolase deficiency
T2 deficiency
ORPHA code
134
OMIM code
203750
ICD10 code
E71.1
ICD11 code
5C50.DY

No additional description.

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